It’s been a year since the gene-editing treatment Casgevy was approved for sickle cell disease and a related blood disorder.

A technique involving the use of light pulses to prevent seizure-like activity in neurons could one day become a new, ...

Harvard Medical School researchers have taken another decisive step in their efforts to develop a gene therapy for people ...

A Northern Ireland woman with a rare condition has admitted that she's looking forward to going completely blind so that her ...