CBL-514 is the first and only drug to receive EMA Orphan Drug Designation for Dercum's disease treatment. - CBL-514 received both FDA Orphan Drug Designation and Fast Track designation for Dercum's ...
An elderly Oklahoma woman stricken with Parkinson’s Disease lost $20,000 in a cryptocurrency ploy that was crafted as a scam ...
Video: Tulsa man with rare muscle disease is gifted a new car and RV to travel the country ...
In Tulsa, mechanic Matt Parker rallied the community to support 21-year-old Corbin Norcom, who has a fatal disease, by ...
A practical calculator that predicts the risk of epilepsy after venous stroke is presented in a study from the University of Gothenburg and others.
Elraglusib has been granted rare pediatric disease designation from the FDA for the treatment of patients with Ewing sarcoma.
Learn why it's making a comeback, its symptoms and what you can do about this disease caused by a vitamin C deficiency.
University of Wisconsin–Madison researchers targeting a group of hereditary neurodegenerative diseases have found success ...
A new treatment that could prevent blindness in children with the CLN2 type Batten disease has been trialed by clinicians and ...
California’s recent decision to create a Rare Disease Advisory Council is a milestone that brings new hope to people living ...
In the wake of an unfavorable advisory committee meeting in September, Intercept Pharmaceuticals’ bid to win full approval ...
California’s recent decision to create a Rare Disease Advisory Council is a milestone that brings new hope to people living ...